Genetic Therapies in Sickle Cell Disease

This webinar provides an overview of genetic therapies — what they are, how they work, and how they may be able to prevent or treat diseases. It also highlights activities of the Cure Sickle Cell Initiative, an NHLBI-led collaborative research effort to accelerate the development of genetic therapies to cure sickle cell disease. And you’ll hear a patient's perspective of participating in clinical trials and the importance of safe and widely available cures. This video is by the National Heart, Lung, and Blood Institute (NHLBI), part of the National Institutes of Health (NIH). Learn more: https://www.nhlbi.nih.gov/grants-and-training Follow us on Twitter: http://www.twitter.com/nih_nhlbi Like us on Facebook: http://www.facebook.com/NHLBI

Science

National Heart, Lung, and Blood Institute

Website

https://www.nhlbi.nih.gov

The National Heart, Lung, and Blood Institute (NHLBI) provides global leadership for a research, training, and education program to promote the prevention and treatment of heart, lung, and blood disorders and enhance the health of all individuals so that they can live longer and more fulfilling lives.

Core Mission Areas

The Science

Discover the goals, challenges, and initiatives that have shaped and will continue to shape prevention, diagnosis, and treatment for the NHLBI’s scientific focus areas.

Clinical Trials

NHLBI-funded clinical trials look at new ways to prevent, detect, or treat disease. The NHLBI is also focused on management and oversight of these trials.